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Papers of the Week

2022 Sep 09

J Pediatr

Maralixibat Treatment Response in Alagille Syndrome Is Associated with Improved Health-Related Quality of Life.


Kamath BM, Goldstein A, Howard R, Garner W, Vig P, Marden JR, Billmyer E, Anderson A, Kirson N, Jacquemin E, Gonzales E
J Pediatr. 2022 Sep 09.
PMID: 36096175.


(s): To assess the impact of treatment response to the ileal bile acid transporter inhibitor maralixibat on health-related quality of life (HRQoL) in children with Alagille syndrome ( ALGS).